Avery's Bucket List: Parents pen blog for baby dying of spinal muscular atrophy

By Sandra Fish Dinakar Singh, chief executive officer of TPG-Axon Capital Management, discusses his daughter Arya's genetic disease and how it led him to establish and fund the Spinal Muscular Atrophy Foundation. You've probably never heard of Spinal

Repligen licensed RG3039 in 2009 from Families of Spinal Muscular Atrophy (FSMA), a patient advocacy organization that funded and directed the preclinical development of RG3039 with an investment of more than $13 million.

But Ryan also goes to physical therapy every other week in an effort to help alleviate the effects of Spinal Muscular Atrophy (SMA), a genetic neuromuscular disease currently with no known treatment or cure. “SMA affects Ryan's balance, core strength,

But Ryan also goes to physical therapy every other week in an effort to help alleviate the effects of Spinal Muscular Atrophy (SMA), a genetic neuromuscular disease currently with no known treatment or cure. “SMA affects Ryan's balance, core strength,

The Fifth Annual Walk n' Roll to cure Spinal Muscular Atrophy (SMA) in honor of Katherine Santiago, will be held Saturday, May 12, at Slayton Field (across.